Lentiviral Gene Therapy with CD34+ Hematopoietic Cells for Hemophilia A

Topics

hemophilia A · lentiviral gene therapy · CD34+ hematopoietic stem cells · factor VIII expression · CD68 promoter · myeloid-directed expression · transduction enhancer · myeloablative conditioning · autologous HSC transplantation · Vector Copy Number · Factor VIII Activity · Annualized Bleeding Rate · Vector Copy Number · engraftment · neutropenia · thrombocytopenia · One-stage assay

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Pepkio Research Index (PRI). Topics and Trends in Most Cited Virus-based gene therapy research Papers, Class of 2026. https://pri.pepkio.com/top-papers/virus-based-gene-therapy-research/2026. Accessed 2026-07-20.

Zheng Su, Tinsley Li, Thematic Shifts in Early-High-Impact Cancer Genomics and Diagnostics Research: A Bibliometric and Semantic Analysis. bioRxiv 2026.07.04.736459; doi: https://doi.org/10.64898/2026.07.04.736459