Gene Editing for <i>CEP290</i> -Associated Retinal Degeneration

Topics

EDIT-101 · CEP290 IVS26 variant · CRISPR-Cas9 gene editing · in vivo gene editing · Subretinal injection · Leber congenital amaurosis · Inherited retinal degeneration · full-field stimulus testing · Best-corrected visual acuity (BCVA) · Ora-Visual Navigation Challenge mobility test · National Eye Institute Visual Function Questionnaire-25 · Children's Visual Function Questionnaire · Photoreceptors · dose-limiting toxicity assessment · photoreceptor gene therapy · BRILLIANCE clinical trial

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Pepkio Research Index (PRI). Topics and Trends in Most Cited Retinal Diseases and Treatments Papers, Class of 2026. https://pri.pepkio.com/top-papers/retinal-diseases-and-treatments/2026. Accessed 2026-07-13.

Zheng Su, Tinsley Li, Thematic Shifts in Early-High-Impact Cancer Genomics and Diagnostics Research: A Bibliometric and Semantic Analysis. bioRxiv 2026.07.04.736459; doi: https://doi.org/10.64898/2026.07.04.736459