Gene Editing for <i>CEP290</i> -Associated Retinal Degeneration
Topics
CEP290 · Inherited retinal degeneration · IVS26 variant · EDIT-101 · CRISPR-Cas9 gene editing · Subretinal injection · Best-corrected visual acuity · Full-field stimulus testing · Ora–Visual Navigation Challenge · National Eye Institute Visual Function Questionnaire–25 · Children's Visual Function Questionnaire · cone-mediated vision · photoreceptor function · in vivo genome editing · Phase 1/2 clinical trial
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Pepkio Research Index (PRI). Topics and Trends in Most Cited Retinal Development and Disorders Papers, Class of 2026. https://pri.pepkio.com/top-papers/retinal-development-and-disorders/2026. Accessed 2026-10-24. Methodology Zheng Su, Tinsley Li, Thematic Shifts in Early-High-Impact Cancer Genomics and Diagnostics Research: A Bibliometric and Semantic Analysis. bioRxiv 2026.07.04.736459; doi: https://doi.org/10.64898/2026.07.04.736459

