Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy
Most Cited Paper
in Metabolism and Genetic Disorders
18 Months Post-Publication
Class of 2026
“Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy”
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Topics
cerebral adrenoleukodystrophy · lentiviral gene therapy · eli-cel · ABCD1 gene · hematopoietic stem cells · major functional disabilities · neurologic function score · magnetic resonance imaging · active inflammation · insertional oncogenesis · myelodysplastic syndrome · allogeneic hematopoietic stem-cell transplantation · viral vector integration · long-term follow-up · Phase 2-3 trial
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Pepkio Research Index (PRI). Topics and Trends in Most Cited Metabolism and Genetic Disorders Papers, Class of 2026. https://pri.pepkio.com/top-papers/metabolism-and-genetic-disorders/2026. Accessed 2026-07-24. Methodology Zheng Su, Tinsley Li, Thematic Shifts in Early-High-Impact Cancer Genomics and Diagnostics Research: A Bibliometric and Semantic Analysis. bioRxiv 2026.07.04.736459; doi: https://doi.org/10.64898/2026.07.04.736459